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Scheie Syndrome - 32 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: A Study Investigating the Relationship Between the Development of Laronidase Antibody and Urinary GAG (Glycosaminoglycan) Levels in Aldurazyme® Treated Patients Condición:
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Enrolling by invitation |
Nombre del estudio: Extension Study of AGT-181-102 to Evaluate Long Term Safety and Activity of AGT-181 Condición: Mucopolysaccharidosis I Fecha: 2015-11-03 Intervenciones: Drug: AGT-181 intravenous infusion over 3-4 hours Ot |
Recruiting |
Nombre del estudio: Biomarker for Patients With Hurler Disease or High-grade Suspicion for Hurler Disease Condición:
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Completed |
Nombre del estudio: A Study of Intrathecal Enzyme Therapy for Cognitive Decline in MPS I Condición:
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Terminated |
Nombre del estudio: Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I Condición:
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Recruiting |
Nombre del estudio: Mucopolysaccharidosis I (MPS I) Registry Condición: Mucopolysaccharidosis I (MPS I) Fecha: 2005-09-02 |
Active, not recruiting |
Nombre del estudio: Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders Condición:
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Recruiting |
Nombre del estudio: Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children Condición:
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